Web Results

www.post-gazette.com/opinion/gene-collier-columns/2020/10/20/Trumpdebate-rules...

Blessedly enough, the final presidential debate is scheduled for Thursday night, and, at least as of my deadline, there was no indication that the last...

finance.yahoo.com/news/gene-therapy-company-aavantibio-launches-113000957.html

* AavantiBio will pursue a diversified gene therapy pipeline, including a lead program in Friedreich’s Ataxia (FA), a rare inherited genetic disease characterized by cardiac and central nervous ...

scitechdaily.com/scientists-restore-vision-in-blind-mice-using-gene-therapy...

Scientists use gene therapy and a novel light-sensing protein to restore vision in mice. NIH-funded therapy will now be tested in humans. A newly developed light-sensing protein called the MCO1 opsin restores vision in blind mice when attached to retina bipolar cells using gene therapy. The Natio

www.eurekalert.org/pub_releases/2020-10/uonc-stm101920.php

Scientists take major step toward Angelman Syndrome gene therapy Published in Nature, research from the UNC School of Medicine shows how gene editing with CRISPR-Cas9 can restore function in an ...

www.thepharmaletter.com/listing/news/gene-therapy?tagid[]=45076

Astellas makes strong move into gene therapy with $3 billion acquisition. 03-12-2019. Astellas Pharma on Monday evening announced that it has entered into a definitive agreement to acquire… Astellas AT132 Audentes Therapeutics Biotechnology Cell and Gene Therapy Companies, mergers and acquisitions Gene therapy Japan USA

www.biophorum.com/phorum/cell-and-gene-therapy/news

News; Sep 2020. On the road to common solutions in cell and gene therapy. The emerging field of cell and gene therapy (CGT) has only recently started being commercialized and so standard methods for generating therapeutic products continue to change. Companies are developing their own procedur...

www.ashclinicalnews.org/spotlight/feature-articles/gene-therapy-hemophilia...

The gene therapy uses Spark’s AAV-LK03 engineered vector, including a liver-specific promoter, to express the human F8 gene, explained the trial’s principal investigator Lindsey George, MD, a physician at the Children’s Hospital of Philadelphia. A total of 14 trial participants received SPK-8011 at one of three dose levels.

www.cbsnews.com/video/could-gene-therapy-cure-sickle-cell-anemia-60-minutes...

An NIH clinical trial is ushering in a genetic revolution as an innovative type of gene therapy is used to attempt to cure sickle cell anemia. Dr. Jon LaPook reports.

www.prnewswire.com/news-releases/sickle-cell-disease-association-of-america-and...

"Now is a perfect time to work with SCDAA to educate the community about gene therapy since we have an open and enrolling phase 1/2 clinical trial for our potentially curative experimental gene ...

www.sciencemag.org/news/2020/01/virus-used-gene-therapies-may-pose-cancer-risk...

Virus used in gene therapies may pose cancer risk, dog study hints. By Jocelyn Kaiser Jan. 6, 2020 , 8:00 AM. Just as gene therapy finally seems to be living up to its promise, a study has revived ...