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www.biopharmadive.com/news/roche-dyno-gene-therapy-deal/586993

Dive Insight: Several recent setbacks notwithstanding, the gene therapy field continues to move forward, with pharmaceutical companies investing in more and more programs while simultaneously searching for ways to make the technology better.. The technical challenges are particularly complex. For instance, the most commonly used gene therapy delivery tool, the adeno-associated virus, has ...

www.republicworld.com/entertainment-news/whats-viral/canada-8-year-old-blind...

An 8-year-old boy in Toronto, Canada became the first patient to be able to see again post a rare gene replacement therapy. According to sources of local CTV, the kid was born with an impaired vision due to a rare genetic disorder called retinitis pigmentosa, which causes mutations in the RPE65 gene.

www.sciencemag.org/news/2020/10/gene-therapy-ready-treat-some-forms-autism

A traditional gene-replacement therapy for Angelman, also funded by FAST, is being tested in animals at the University of Pennsylvania, according to James Wilson, who directs the Gene Therapy ...

www.thepharmaletter.com/listing/news/gene-therapy?tagid[]=45076

Astellas makes strong move into gene therapy with $3 billion acquisition. 03-12-2019. Astellas Pharma on Monday evening announced that it has entered into a definitive agreement to acquire… Astellas AT132 Audentes Therapeutics Biotechnology Cell and Gene Therapy Companies, mergers and acquisitions Gene therapy Japan USA

www.newsbreak.com/topics/gene-therapy-work

News Break; gene therapy work. GENE THERAPY WORK. techstartups.com | 09-16. Gene-editing biotech startup Graphite Bio launches with $45 million Series A funding to treat a broad range of severe diseases.

parkinsonsnewstoday.com/2020/10/08/gene-therapy-axo-lenti-pd-showing-benefit...

AXO-Lenti-PD, a gene therapy being developed by Axovant, uses a viral vector to deliver three genes involved in the production of dopamine (tyrosine hydroxylase, cyclohydrolase 1, and aromatic L-amino acid decarboxylase) to brain cells via a surgical procedure.The therapy’s overall goal is to restore steady dopamine levels in the brain. SUNRISE-PD, a Phase 1/2 clinical trial (NCT03720418 ...

musculardystrophynews.com/2020/10/08/pfizers-duchenne-gene-therapy-placed-on...

The U.S. Food and Drug Administration (FDA) has granted fast track designation to PF-06939926, Pfizer’s investigational gene therapy for Duchenne muscular dystrophy (DMD).. This designation is given to treatments that show considerable potential in addressing serious conditions for which available treatments fall short.

hemophilianewstoday.com/2020/09/30/crispr-cas9-may-be-superior-to-conventional...

The gene-editing tool CRISPR/Cas9 may be superior to conventional gene therapy at increasing the activity of artificial factor IX (FIX), the blood-clotting protein missing in people with hemophilia B, according to a study in primates by Intellia Therapeutics.. Using a mouse model of liver regeneration, Intellia investigators also showed that when CRISPR/Cas9 is used to insert the human version ...

www.cbsnews.com/video/could-gene-therapy-cure-sickle-cell-anemia-60-minutes...

An NIH clinical trial is ushering in a genetic revolution as an innovative type of gene therapy is used to attempt to cure sickle cell anemia. Dr. Jon LaPook reports.

www.genetherapynet.com

Gene Therapy Net is the web resource for patients and professionals interested in gene therapy.The objectives of Gene Therapy Net are to be the information resource for basic and clinical research in gene therapy, cell therapy, and genetic vaccines, and to serve as a network in the exchange of information and news related to above areas.