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telanganatoday.com/whats-sma-disease-that-is-affecting-kids-and-why-is-treatment-so-expensive

Jul 1, 2021 ... Ayaansh Gupta is just 3-years-old. But he became one of the first patients in Hyderabad to be administered Zolgensma, a gene therapy with a ...

www.mma.org/gene-therapies-offer-breakthrough-results-but-extraordinary-costs

Mar 18, 2020 ... As a result, many patients are either denied gene therapy treatments or they experience lengthy delays in receiving coverage.

smanewstoday.com/news-posts/2019/01/04/zolgensma-cost-effective-spinraza-2-million-price-icer-report-says

Jan 4, 2019 ... ... (SMA) treatment Zolgensma (onasemnogene abeparvovec-xxxx) could be more cost-effective than Spinraza (nusinersen) with a one-time price ...

news.sky.com/story/worlds-most-expensive-drug-licensed-for-use-on-nhs-at-price-fair-to-taxpayers-12239862

Mar 8, 2021 ... Zolgensma has a reported list price of nearly £1.8m per dose, ... is why NHS England has moved mountains to make this treatment available, ...

journals.lww.com/neurotodayonline/fulltext/2019/04180/two_new_treatments_for_spinal_muscular_atrophy_may.8.aspx

Apr 18, 2019 ... The agency does not assess what the drug is worth for an individual patient or family; it considers the cost-effectiveness of drugs from a ...

www.washingtonpost.com/business/economy/the-costliest-drug-on-the-planet-will-treat-infants-with-rare-disease-the-market-fight-focused-on-cost-and-safety-is-just-getting-started/2019/05/15/aa4bb4d8-6ce8-11e9-8f44-e8d8bb1df986_story.html

May 15, 2019 ... Now, the Food and Drug Administration is poised to approve a second gene treatment for infants with SMA, and with a price tag of $1.5 million to ...

xconomy.com/national/2019/05/02/sma-moment-will-gene-therapy-shift-treatment-costs-of-muscle-disease

May 2, 2019 ... This is a big moment for people diagnosed with spinal muscular atrophy, or SMA, a rare and potentially lethal genetic disorder that destroys ...

www.fool.com/investing/2019/05/30/bothered-by-the-price-tag-of-a-24-million-drug-rea.aspx

May 30, 2019 ... There's only one other approved treatment for SMA, Biogen's Spinraza. The drug costs $750,000 in year one and $375,000 for every subsequent ...

www.xcenda.com/insights/htaq-fall-2019-the-cost-of-cures-zolgensma-cea

Oct 29, 2019 ... On May 24, 2019, the United States (US) Food and Drug Administration (FDA) approved ZOLGENSMA (onasemnogene abeparvovec), a 1-time treatment ...

www.webmd.com/brain/spinal-muscular-atrophy

Nov 4, 2020 ... There are different types of SMA, and how serious it is depends on which type your child has. There's no cure, but treatments can improve some ...

www.bcbsla.com/landing/gene-therapy

Today, the average wholesale cost of Zolgensma is $2.125 million* for a ... and other criteria as gene therapy treatments like these enter the market.